CHAPTER 10

A gene mutation is when a hereditary change occurs in the gene message causing a particular phenotype. It typically cannot be visualized microscopically. It is usually referred to as a point mutation. It typically involves a single base or a small cluster of nearby bases. Point mutations may be:

Base substitutions- where one base pair is replaced by another. A base substitution may be a transition (purine replaces purine and pyrimidine replaces pyrimidine), or a transversion (a purine replaces a pyrimidine or vice versa).

Additions or Deletions- a base pair is added or eliminated from the previous message.Often these are referred to as Indel mutations. These usually lead to frame shift mutations which scramble the message downstream from the location of the addition or deletion. Often this causes a translational termination (stop) signal to arise prematurely in the mRNA message.

Mutations are described as synonymous if they represent redundant codons for the same amino acid, missense if they represent codons for different amino acids, or nonsense if they replace a codon for an amino acid with a stop signal.

Conservative substitutions replace one amino acid by another with similar properties and are likely to have less severe phenotypic effects than nonconservative substitutions.

Mutations may affect coding regions of DNA or noncoding regions (e.g., regulatory regions).

If mutations occur in response to a known environmental cause or due to treatment with a mutagen they are classified as induced mutations. Mutations that can not be attributed to known mutagens reflect background mutational levels and are referred to as spontaneous mutations. Spontaneous mutations occur at the rate of 10-5 to 10-8. When researchers attempt to induce mutations they assume that all mutations that occur are the result of induction and disregard the low levels of mutations that are spontaneous.

Tautomerization

Each base can occur in either of two states and relative frequency of these two states is in equilibrium for each base. The most significant thing to remember about these states is that the rare forms will have different pairing properties than the common forms, BUT the rare form will be a purine if the common form is a purine and a pyrimidine if the common form is a pyrimidine. Therefore, if a base spontaneously takes on its rare tautomeric form during replication a transition mutation results. Figure 10-6.

Base Analogues are compounds that are sufficiently similar to normal nitrogenous bases that they may be incorporated in nucleotides in the place of the normal nitrogenous bases. These base analogues often will undergo tautomeric shifts with greater frequency than the normal bases leading to transitional mutations. These are commonly used for inducing mutations. See 5-bromouracil (5-Bu) in Figure 10-8 and 2-Aminopurine (2-AP) in Figure 10-9. %-Bu in its common form displaces Thymine, but in its tautomeric form pairs with Guanine. 2-AP will displace Adenine and miss pair with Cytosine.

Base Alteration. Some mutagens are not incorporated into the DNA, but alter the existing base. Alkylating agents (e.g., ethylmethanesulfonate ( EMS ): causes guanine to pair with thymine). Figure 10-10.

Intercalating agents: (e.g., proflavin, acridine orange) fit into the DNA double helix between adjacent base pairs leading to frame shifts.

Base damage can prevent replication under some circumstances. This must be avoided at all costs by organisms or they will be doomed. Some bacteria have an SOS system that responds to such situations and reduce the fidelity of fidelity of positioning complementary bases opposite the sites with damage. UV radiation induces dimer formation and may stimulate the SOS response. Aflotoxin B1 (Figure 10-15) causes guanine to break off from the deoxyribose sugar thereby creating an apurinic site (Figure 10-16). The SOS response is elicited in this case and typically places an adenine opposite the apurinic site (a transversion).

Deamination of cytosine yields uracil which will pair with adenine leading to a transition mutation. However, uracil-DNA glycosylase usually recognizes uracil in the DNA and removes them. Often cytosine is methylated in eukaryotes forming 5-methylcytosine. When this is deaminated it pairs with thymine and the consequent transition. Figure 10-17. Methylated cytosine represents a hot spot for mutations because thymine is not recognized as an inappropriate base in DNA by any DNA glycosylase (Figure 10-18).

Some oxygen species can cause oxidative damage to bases (Figure 10-19). These may lead to transversions.

Trinucleotide repeats are common and they are frequently associated with human genetic diseases in individuals having too many copies. Often the parents have more copies of the trinucleotide repeats than is typical and this leads to slippage during replication producing many more copies in affected individuals.

Transposable elements can disrupt the normal coding messages for polypeptides if they are inserted within the coding region of a gene and alternatively they can modify the rate at which a gene is transcribed when inserted in the regulatory region for a gene.

Biological Repair mechanisms

When DNA is being replicated initially incorrect base pairing is not uncommon. During DNA replication, mismatched nucleotides are incorporated at the rate of 10-5 per template nucleotide per round of replication. DNA polymerase has an additional function beyond synthesizing the polymer; it has proof reading responsibility. It has 3' to 5' exonuclease activity that permits it to eliminate most incorrectly positioned bases soon after they are added to the growing sugar phosphate backbone. About 99% of the initially mismatched nucleotides are corrected via proof reading. Mismatch repair (see below) corrects 99.9% of the remaining mismatches.

Another method for preventing errors is via the enzyme superoxide dismutase which converts superoxide radicals to hydrogen peroxide (H2O2) which is then converted to water (H2O) by the enzyme catalase.

Lesions to DNA consisting of pyrimidine dimers can be repaired by the enzyme photolyase in bacteria and lower eukaryotes. Photolyase can only function if it is exposed to visible light during repair.

Alkyltransferases are enzymes that reverse lesions caused by alkylating agents.

The general excision repair system can recognize significant DNA lesions (e.g., thymine dimers) and use endonuclease activity to break the sugar phosphate phosphodiester bonds up and down stream from the lesion. This allows the problem area to be excised from the DNA. The excised gap is 12 or 13 nucleotides in prokaryotes, 27-29 nucleotides in eukaryotes. This strand is resynthesized using DNA polymerase I and the strand is sealed using a ligase.

The specific excision repair involves repair of less obvious lesions in the DNA. DNA glycosylases recognize altered bases and cleave the base from its sugar thereby creating an AP site. AP sites are recognized by AP endonucleases which then excise the AP site and replace it with an appropriate nucleotide using DNA polymerase I and a ligase.

Mismatch repair occurs soon after the DNA is replicated. Incorrectly matched base pairs are recognized and the incorrect nucleotide is excised and replaced by a correct nucleotide. The difficulty in this system is identifying which strand contains the incorrect nucleotide. This is done in prokaryotes by taking advantage of the fact that when a DNA sequence 5'GATC3' occurs, the adenine will be methylated in prokaryotes. However, this methylation occurs post-replication. Therefore, there is a short period of time during which only one of the two DNA strands is methylated and this represents the older strand and the one with the correct sequence. The methylation site does not have to exist extremely near the mismatch.

Recombinational repair is a process that occurs post replication. When a strand containing a major DNA lesion is to be replicated the complement is synthesized in such a way that a gap is left opposite the region containing the lesion. The details concerning how this is done by DNA polymerase have yet to be worked out. After replication, a region of the other DNA strand in the original DNA molecule is used to fill in the missing gap. Now the other original strand is missing a gap. This gap is synthesized by using its newly synthesized complement as a template. See Figure 10-41.

Mutations may be somatic or germinal in nature. We are most concerned about germinal mutations because they are passed from generation to generation. Somatic mutations may affect inheritance in plants when they occur in branches that give rise to flowers that become part of the reproductive system of the organism. They also can be important for asexual species.

Most mutations are recessive. They can only be recognized if they do not coexist with a dominant form in a diploid individual. Therefore, to recognize that a mutation has been induced in a subject often that subject is test crossed. This type of mutation detection is called a specific-locus test.

A mutation from wild type to mutant form is referred to as a forward mutation. A mutation from mutant form to wild type is a back (or reverse) mutation.

A conditional mutant allele causes the mutant phenotype only in a certain environment, called the restrictive condition. The wild type phenotype is produced in other environments (permissive conditions). Some mutant alleles can only influence phenotypes if the individual exists in the restrictive condition during a particular period of its development (sensitive period).